Trials
This page lists the trials into DMD and BMD in the UK that are currently recruiting, using the DMD Register, and what the recruitment criteria are. If you wish to be considered for a trial please contact Action Duchenne.
PTC124 in DMD (UK) Phase 2b
| Phase | Drug | Min Age | Max Age | Enrollment | Status |
|---|---|---|---|---|---|
| Phase 2 | PTC-124 | 5 | - | 100 | Recruiting |
Locations: Dubowitz Neuromuscular Centre, Hammersmith Hospital and Institute of Human Genetics, Newcastle upon Tyne
Safety and Efficacy Study of Antisense Oligonucleotides in Duchenne Muscular Dystrophy (Exon 51)
| Phase | Drug | Min Age | Max Age | Enrollment | Status |
|---|---|---|---|---|---|
| Phase 1 & 2 | AVI-4658 | 12 | 17 | 9 | Recruiting |
Locations: Dubowitz Neuromuscular Centre, Hammersmith Hospital and Clinical Trails Unit, St Mary's Hospital
Pre-Study Assessment for Systemic Antisense Oligonucleotides in Duchenne Muscular Dystrophy (Exon 51 and 53)
| Phase | Drug | Min Age | Max Age | Enrollment | Status |
|---|---|---|---|---|---|
| Not Applicable | AVI-4658 | 5 | 12 | - | Recruiting |
Locations: Dubowitz Neuromuscular Centre, Hammersmith Hospital and Clinical Trails Unit, St Mary's Hospital

