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Trials

This page lists the trials into DMD and BMD in the UK.

PTC124 in DMD (UK) Phase 2b

Phase Drug Min Age Max Age Enrollment Status
Phase 2 PTC-124 5 - 100 Recruiting

Locations: Dubowitz Neuromuscular Centre, Hammersmith Hospital and Institute of Human Genetics, Newcastle upon Tyne

Safety and Efficacy Study of Antisense Oligonucleotides in Duchenne Muscular Dystrophy (Exon 51)

Phase Drug Min Age Max Age Enrollment Status
Phase 1 & 2 AVI-4658 12 17 9 Recruiting

Locations: Dubowitz Neuromuscular Centre, Hammersmith Hospital and Clinical Trails Unit, St Mary's Hospital

Pre-Study Assessment for Systemic Antisense Oligonucleotides in Duchenne Muscular Dystrophy (Exon 51 and 53)

Phase Drug Min Age Max Age Enrollment Status
Not Applicable AVI-4658 5 12 - Recruiting

Locations: Dubowitz Neuromuscular Centre, Hammersmith Hospital and Clinical Trails Unit, St Mary's Hospital

Action Duchenne

The DMD Registry is sponsored and controlled by Action Duchenne UK Limited (Action Duchenne Ltd), and has been registered under the Data Protection Act (1998).

Treat NMD

The DMD Registry is part of the Treat-NMD Network.

The DMD Registry - Helping to win the race against time